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Clinical Neurology · Neuro-Immunology

Choosing an Immunomodulator

Selecting an immunomodulator depends on the underlying disease, the goal of chronic (maintenance) immunotherapy, and pregnancy considerations.

Preferred agents by disease

DiseaseChronic (maintenance) immunotherapy
CIDPSteroids, azathioprine, mycophenolate, cyclosporine
MMNMonthly IVIG, rituximab, cyclophosphamide
Anti-MagRituximab, cyclophosphamide
PolymyositisSteroids, azathioprine, rituximab
MyastheniaSteroids, azathioprine, mycophenolate, cyclosporine, tocilizumab, rituximab
NMORituximab, mycophenolate, azathioprine, eculizumab (Mayo Clinic trial)
ParaneoplasticSteroids, monthly IVIG, rituximab
GCA (arteritis)Steroids, tocilizumab

Rituximab

  • Used for: CIDP, Anti-Mag, MMN, inflammatory myopathies, myasthenia gravis, RRMS, NMO & paraneoplastic syndromes.
  • Phase I and II studies on rituximab for MS patients showed marked success; however the manufacturer didn't seek FDA approval.
  • Infusion-related reactions are thought to be related to its cytolytic effect on CD20 cells with release of cytokines.
  • Rituximab protocol is available at http://neurologyresidents.com/neuro-immunology

Pregnancy category

ClassAgents
Class BNone
Class CRituximab, steroids, IVIG, cyclosporine, tacrolimus
Class DCyclophosphamide, azathioprine, mycophenolate
Class XMethotrexate
Not assignedTocilizumab

Ahmed Koriesh, MD