← Back
NeuroTrials.ai
Neurology Clinical Trial Database

LATTICE

Low-Dose Lithium for Mild Cognitive Impairment: A Pilot Randomized Clinical Trial

Year of Publication: 2026

Authors: Gildengers AG, Ibrahim TS, Anderson SJ, et al.

Journal: JAMA Neurology

Citation: JAMA Neurol. 2026;83(4):310-319

Link: https://doi.org/10.1001/jamaneurol.2026.0072


Clinical Question

Does low-dose lithium slow cognitive decline and preserve brain volume in adults with mild cognitive impairment?

Bottom Line

Low-dose lithium (150-300 mg daily) did not meet any of its 6 coprimary endpoints over 2 years in adults with MCI. A nominally significant verbal memory benefit (P=0.05) and a numerical trend toward hippocampal preservation were observed but fell short of the prespecified threshold. Larger effects in amyloid-positive participants warrant further investigation in enriched populations.

Major Points

  • None of the 6 coprimary endpoints reached the prespecified P<0.01 significance threshold -- the trial's primary result is negative.
  • CVLT-II verbal memory showed the strongest signal: lithium reduced annual decline by ~49% (0.73 vs 1.42 pts/year, diff 0.69, 95% CI 0.01-1.37, P=0.05) -- nominally significant but below threshold.
  • Hippocampal volume loss was numerically less with lithium (59 mm3/year difference, P=0.09) -- a trend without significance.
  • Amyloid-positive subgroup showed larger effect sizes: Hedges g=0.74 for verbal memory and g=0.82 for hippocampal volume, suggesting potential benefit in those with underlying Alzheimer pathology.
  • SAEs occurred in 29% lithium vs 23% placebo; none were considered definitely treatment-related, supporting tolerability of low-dose lithium.
  • As a single-site pilot trial (n=80), the study was underpowered -- results are hypothesis-generating and should not change clinical practice.
  • Findings support a larger RCT enriched for amyloid-positive MCI participants to adequately test lithium as a disease-modifying agent.

Design

Study Type: Single-center, randomized, double-blind, placebo-controlled pilot trial

Randomization: 1

Blinding: Double-blind (participants and investigators blinded to treatment assignment)

Allocation: 1:1

Enrollment Period: February 2018 - August 2024

Follow-up Duration: 2 years

Centers: 1

Countries: USA

Sample Size: 83

Analyzed: 80

Analysis: Mixed-effects model for repeated measures (MMRM)

Power Calculation: Powered to detect medium effect sizes (d=0.5) for each coprimary outcome at P<0.01


Inclusion Criteria

  • Age 55-90 years
  • Diagnosis of mild cognitive impairment (MCI)
  • Stable medical status permitting 2-year participation

Exclusion Criteria

  • Current or prior use of lithium
  • Significant renal or thyroid disease
  • Current dementia diagnosis
  • Significant psychiatric illness requiring medication change

Arms

FieldLithiumControl
N4139
InterventionLithium carbonate 150 mg daily, titrated to 300 mg daily as tolerated, taken orallyMatching placebo capsule taken orally daily
Duration2 years2 years

Outcomes

OutcomeTypeControlInterventionHR / OR / RRP-value
6 coprimary outcomes at 2 years: (1) CVLT-II verbal memory composite, (2) BVMT-R visual memory composite, (3) PACC global cognitive composite, (4) hippocampal volume, (5) cortical gray matter volume, (6) serum BDNF -- all assessed over 2 years using MMRMPrimaryNone of 6 outcomes met thresholdNone of 6 outcomes met thresholdAll P>0.01
CVLT-II verbal memory -- annual rate of declineSecondary1.42 pts/year decline0.73 pts/year decline0.05
Hippocampal volume -- annual rate of changeSecondaryGreater annual loss59 mm3/year less loss than placebo0.09
BVMT-R visual memory compositeSecondary>0.01
PACC global cognitive compositeSecondary>0.01
Cortical gray matter volumeSecondary>0.01
Serum BDNFSecondary>0.01
Amyloid-positive subgroup -- CVLT-II effect sizeSecondaryHedges g=0.74 (exploratory)
Amyloid-positive subgroup -- hippocampal volume effect sizeSecondaryHedges g=0.82 (exploratory)
Serious adverse events (SAEs)Safety23%29%
Serious Adverse EventsAdverse23%29%

Subgroup Analysis

Amyloid-positive participants showed larger effect sizes compared to the overall cohort: Hedges g=0.74 for CVLT-II verbal memory and g=0.82 for hippocampal volume, suggesting that lithium may have greater neuroprotective benefit in individuals with underlying Alzheimer amyloid pathology. This was an exploratory post-hoc analysis.


Criticisms

  • Single-site pilot trial with limited statistical power and generalizability
  • 6 coprimary endpoints without adequate multiple comparison correction inflate false-positive risk
  • Small sample size (n=80) means most individual endpoints are severely underpowered
  • Dose titration from 150 to 300 mg introduces variability in exposure
  • Amyloid subgroup analysis was exploratory and based on a subset of participants -- highly susceptible to type I error
  • The 2-year follow-up may be insufficient to detect disease modification effects in MCI

Funding

National Institute on Aging (R01 AG055389)

Based on: LATTICE (JAMA Neurology, 2026)

Authors: Gildengers AG, Ibrahim TS, Anderson SJ, et al.

Citation: JAMA Neurol. 2026;83(4):310-319

Content summarized and formatted by NeuroTrials.ai.