← Back
NeuroTrials.ai
Neurology Clinical Trial Database

FASTEST

Recombinant factor VIIa versus placebo for spontaneous intracerebral haemorrhage within 2 h of symptom onset (FASTEST): a multicentre, double-blind, randomised, placebo-controlled, phase 3 trial

Year of Publication: 2026

Authors: Broderick JP, Naidech AM, Elm JJ, ..., for the FASTEST Investigators

Journal: The Lancet

Citation: Lancet. 2026;407:773-783

Link: https://doi.org/10.1016/S0140-6736(26)00097-8


Clinical Question

Does recombinant factor VIIa given within 2 hours of ICH onset improve functional outcomes compared to placebo?

Bottom Line

Recombinant factor VIIa 80 µg/kg given within 2 hours of ICH onset significantly slowed haematoma growth but did not improve functional outcomes at 180 days and was associated with a 3-fold increased risk of life-threatening thromboembolic events. The trial was stopped for futility. Subgroup signals in patients with a CT spot sign or treated within 90 minutes are hypothesis-generating and being investigated in FASTEST part 2.

Major Points

  • No improvement in functional outcome: mRS distribution at 180 days was identical between groups (OR 1.09, 95% CI 0.79-1.51, p=0.61); trial stopped for futility at second interim analysis (conditional power <1%).
  • rFVIIa significantly slowed haematoma growth: ICH volume change from baseline to 24h was -3.7 mL less with rFVIIa (p=0.0011) and ICH+IVH growth was -5.2 mL less (p=0.0011).
  • Slowing bleeding did not translate to improved outcomes, suggesting that a mean reduction of ~3-4 mL may be insufficient; modelling suggests 6-12 mL may be needed to improve functional outcomes.
  • Life-threatening thromboembolic complications within 4 days were significantly higher with rFVIIa: 15 (<5%) vs 4 (1%), RR 3.41 (95% CI 1.14-10.15, p=0.020).
  • Subgroup signals (non-significant but prespecified): spot sign OR 1.86 (0.94-3.68) and treatment within 90 min OR 1.82 (0.98-3.40) -- patients with both features showed the greatest exploratory benefit.
  • Adaptive enrichment to age <=70 years was added during the trial but also showed no benefit (conditional power <1%).
  • FASTEST part 2 (NCT07227246) is ongoing, recruiting additional sites specifically targeting patients with a spot sign or treated within 90 min.
  • CT angiography should be integrated into standard ICH assessment workflows to rapidly identify patients with spot signs and ongoing bleeding risk.

Design

Study Type: Multicentre, double-blind, randomised, placebo-controlled, adaptive, phase 3 trial

Randomization: 1

Blinding: Double-blind (all investigators and participants masked)

Allocation: 1:1 (step-forward randomisation using lowest pre-randomised kit at a site)

Enrollment Period: December 3, 2021 – October 1, 2025

Follow-up Duration: 180 days

Centers: 93

Countries: USA, Japan, Canada, Spain, Germany, UK

Sample Size: 626

Analyzed: 626

Analysis: Ordinal logistic regression for primary outcome, adjusted for age, baseline ICH volume, baseline IVH volume, pre-stroke mRS; modified ITT

Power Calculation: 388 participants per group (860 total) for 80% power to detect 10% absolute difference in mRS 0-2 at 90 days; adaptive re-estimation allowed up to 1330 participants

Registration: NCT03496883; EudraCT 2019-003722-25; EU CTR 2024-517383-28-00


Inclusion Criteria

  • Age 18-80 years
  • Spontaneous ICH 2-60 mL on baseline CT
  • IVH in less than two-thirds of one lateral ventricle or less than one-third of both lateral ventricles
  • Glasgow Coma Scale score at least 8
  • No evidence of recent ischaemic stroke or myocardial infarction (past 90 days)
  • No anticoagulation use within the past 7 days
  • No other structural cause of ICH
  • Treated within 2 hours of stroke onset or last known well

Exclusion Criteria

  • Ischaemic stroke or MI within past 90 days
  • Recent anticoagulation use within 7 days
  • Known structural cause of ICH (AVM, aneurysm, tumour, etc.)
  • Planned neurosurgical evacuation within 24 hours of enrollment
  • Pregnancy
  • ICH volume >60 mL or <2 mL
  • Significant IVH (>2/3 of one lateral ventricle or >1/3 of both)

Arms

FieldRecombinant factor VIIaControl
N328298
InterventionRecombinant factor VIIa 80 µg/kg IV over 2 min (maximum dose 10,000 µg or 10 mg)Identical volume placebo (same solvent and process) IV over 2 min
DurationSingle doseSingle dose

Outcomes

OutcomeTypeControlInterventionHR / OR / RRP-value
Ordinal modified Rankin Scale (mRS 0-2, 3, and 4-6) at 180 days, measured by Rankin Focused Assessment Tool; analysed by ordinal logistic regressionPrimary134/298 (45%) mRS 0-2; 76/298 (26%) mRS 3; 88/298 (30%) mRS 4-6151/328 (46%) mRS 0-2; 80/328 (24%) mRS 3; 97/328 (30%) mRS 4-61.090.61
mRS 0-2 at 90 daysSecondary113/298 (38%)132/328 (40%)0.87
mRS 0-2 at 180 daysSecondary134/298 (45%)151/328 (46%)0.87
Change in ICH volume from baseline to 24h (mL)Secondary5.5 mL (SD 13.7)1.9 mL (SD 7.0)0.0011
Change in ICH plus IVH volume from baseline to 24h (mL)Secondary7.4 mL (SD 19.6)2.2 mL (SD 8.4)0.0011
All-cause mortality at 180 daysSecondary22 (7%)20 (6%)
Subgroup: mRS at 180 days -- spot sign presentSecondary77 patients71 patientsNS (exploratory)
Subgroup: mRS at 180 days -- treated within 90 minSecondary92 patients82 patientsNS (exploratory)
Life-threatening thromboembolic complications within 4 days (primary safety)Safety4 (1%)15 (<5%)0.020
Life-threatening thromboembolic complications within 90 daysSafety11 (4%)21 (6%)0.15
Life-threatening thromboembolic events within 4 daysAdverse4 (1%)15 (<5%)3.410.020
Deep venous thrombosisAdverse4 (1%)7 (2%)1.59
Acute myocardial infarctionAdverse4 (1%)3 (1%)0.68
Acute cerebral infarctionAdverse11 (4%)18 (5%)1.49
Acute pulmonary embolismAdverse3 (1%)5 (2%)1.51
Mortality at 180 daysAdverse22 (7%)20 (6%)0.83

Subgroup Analysis

No prespecified subgroup analysis reached statistical significance. Prespecified subgroup signals favoring rFVIIa (non-significant): spot sign present (OR 1.86, 95% CI 0.94-3.68) and treatment within 90 min (OR 1.82, 95% CI 0.98-3.40). Exploratory analysis showed the greatest potential benefit in patients with both a spot sign AND treatment within 90 min. Post-hoc logistic regression interaction modelling suggested patients with both features may derive meaningful functional benefit. These findings are being prospectively tested in FASTEST part 2 (NCT07227246). Age (<=70 vs >70 years), country/region, ultra-early haematoma growth rate, and ICH volume subgroups showed no differential benefit.


Criticisms

  • Trial stopped early for futility -- underpowered for subgroup analyses, which remain exploratory
  • Mean haematoma growth reduction (~3.5 mL) appears insufficient; modelling suggests 6-12 mL may be needed to improve functional outcomes
  • Thromboembolic risk is a real and significant concern -- limits widespread use even if efficacy were confirmed
  • Asian patients comprised ~55% of the sample (due to Japan enrollment); findings may not be fully generalisable to other populations given different ICH etiologies (hypertensive-dominant in Japan vs more diverse in USA)
  • Adaptive enrichment to younger patients (<=70 years) was added mid-trial but also showed no benefit, reducing confidence in age-based patient selection
  • Only 45% of participants received treatment within 90 min or had a spot sign -- the 'ideal' subgroup was a minority, limiting the ability to test these hypotheses definitively
  • Emergency consent procedures and mobile stroke units add operational complexity not universally available

Funding

National Institute of Neurological Diseases and Stroke (NINDS); Japan Agency for Medical Research and Development (AMED); Novo Nordisk (supply of study medication)

Based on: FASTEST (The Lancet, 2026)

Authors: Broderick JP, Naidech AM, Elm JJ, ..., for the FASTEST Investigators

Citation: Lancet. 2026;407:773-783

Content summarized and formatted by NeuroTrials.ai.