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CANNABIS MIGRAINE

Vaporized Cannabis versus Placebo for Acute Migraine: A Randomized Controlled Trial

Year of Publication: 2024

Authors: Nathaniel M. Schuster, Mark S. Wallace, Thomas D. Marcotte, ..., Michelle Sexton

Journal: medRxiv (preprint)

Citation: Schuster NM, Wallace MS, Marcotte TD, Buse DC, Lee E, Liu L, Sexton M. Vaporized Cannabis versus Placebo for Acute Migraine: A Randomized Controlled Trial. medRxiv. 2024. doi:10.1101/2024.02.16.24302843

Link: https://doi.org/10.1101/2024.02.16.24302843


Clinical Question

Is vaporized cannabis (THC-dominant, CBD-dominant, or THC+CBD) superior to placebo for the acute treatment of migraine attacks?

Bottom Line

Vaporized 6% THC+11% CBD cannabis flower was superior to placebo for 2-hour pain relief, pain freedom, and MBS freedom, with sustained benefits at 24 and 48 hours and no serious adverse events — the first RCT evidence supporting cannabinoid use for acute migraine.

Major Points

  • THC+CBD (6% THC + 11% CBD) was superior to placebo for 2-hour pain relief (67.2% vs 46.6%, OR 2.85 [1.22–6.65], p=0.016), 2-hour pain freedom (34.5% vs 15.5%, OR 3.30 [1.24–8.80], p=0.017), and 2-hour MBS freedom (60.3% vs 34.5%, OR 3.32 [1.45–7.64], p=0.005).
  • THC+CBD achieved superior sustained benefits: 24-hour sustained pain freedom (28.0% vs 10.7%, OR 3.45 [1.14–10.50], p=0.029), 24-hour sustained MBS freedom (46.0% vs 25.0%, OR 2.83 [1.10–7.26], p=0.031), and 48-hour sustained MBS freedom (39.6% vs 18.4%, OR 3.39 [1.24–9.32], p=0.018).
  • THC-dominant (6% THC) was superior to placebo for 2-hour pain relief (68.9% vs 46.6%, OR 3.14 [1.35–7.30], p=0.008) but not for 2-hour pain freedom or MBS freedom, and showed no sustained benefit at 24 or 48 hours.
  • CBD-dominant (11% CBD) was not superior to placebo for any primary or secondary 2-hour endpoint.
  • At 1 hour, all three active arms achieved superior pain relief vs placebo (THC+CBD 53.6%, THC-dominant 65.5%, CBD-dominant 58.9% vs placebo 36.7%); only THC-dominant achieved superior 1-hour pain freedom (17.2% vs 5.0%, OR 4.90, p=0.034).
  • THC+CBD reduced photophobia and phonophobia at 2 hours but not nausea or vomiting, arguing against a purely antiemetic mechanism.
  • THC+CBD produced less subjective highness (2.4/10 vs 3.5/10 at 1 hour), euphoria, and cognitive impairment than THC-dominant, consistent with CBD acting as a negative allosteric modulator of CB1.
  • Blinding was well maintained — participants correctly identified their treatment at rates near or below chance across all arms.
  • No serious adverse events were reported across 247 treated attacks.
  • This is the first randomized, double-blind, placebo-controlled trial establishing efficacy of cannabinoids for the acute treatment of migraine.

Design

Study Type: Randomized, double-blind, placebo-controlled, 4-treatment crossover trial

Randomization: 1

Blinding: Quadruple-blind (participants, research coordinators, investigators, and statisticians); only research pharmacists were unblinded

Allocation: Simple 1:1:1:1 assignment across 24 possible treatment orders, randomized by research pharmacist using Microsoft Excel random number function

Enrollment Period: November 20, 2020 – November 4, 2022; follow-up completed February 23, 2023

Follow-up Duration: 48 hours per treated migraine attack; ≥1 week washout between treated attacks; up to 4 attacks treated per participant

Centers: 1

Countries: United States

Sample Size: 92

Analyzed: 73

Analysis: Intention-to-treat (ITT; 247 attacks, 73 participants), modified ITT (mITT; 234 attacks, 71 participants), and sensitivity analysis (202 attacks, 70 participants); generalized linear mixed effects model with logit link for binary outcomes and random intercept to account for within-subject clustering

Power Calculation: 72 participants needed for 80% power to detect difference in pain relief (68% vs 45% assumed, based on intranasal sumatriptan RCT); 90 planned to allow for 20% dropout

Registration: NCT04360044


Inclusion Criteria

  • Ages 21–65
  • Migraine diagnosis per ICHD-3 criteria
  • 2–23 headache days per month
  • 2–23 migraine days per month
  • Agreement to avoid non-study cannabis, opioids, and barbiturates during study participation

Exclusion Criteria

  • Positive urine drug screen at screening for THC, barbiturates, opioids, oxycodone, or methadone
  • Pregnancy or breastfeeding
  • Known cognitive impairment
  • Current moderate-severe or severe depression
  • History of bipolar disorder, schizophrenia, or psychosis
  • History of substance use disorder
  • Active pulmonary disease or other severe medical illnesses at researcher discretion

Arms

FieldTHC+CBDTHC-dominantCBD-dominantControl
N58615758
InterventionVaporized cannabis flower 6.16% THC + 10.77% CBD (referred to as 6% THC+11% CBD); 4 puffs via Foltin Uniform Puff Procedure (FUPP) at 180°C per qualifying migraine attack; N reflects mITT attacksVaporized cannabis flower 5.62% THC + 0.03% CBD (referred to as 6% THC-dominant); 4 puffs via FUPP at 180°C per qualifying migraine attack; N reflects mITT attacksVaporized cannabis flower 11.27% CBD + 0.35% THC (referred to as 11% CBD-dominant); 4 puffs via FUPP at 180°C per qualifying migraine attack; N reflects mITT attacksVaporized placebo cannabis flower (<0.025% THC + 0.14% CBD), THC and CBD extracted via chemical process by NIDA Drug Supply Program; 4 puffs via FUPP at 180°C per qualifying migraine attack; N reflects mITT attacks
DurationSingle-dose per qualifying migraine attack (crossover — each participant received this treatment for one of up to 4 attacks)Single-dose per qualifying migraine attack (crossover)Single-dose per qualifying migraine attack (crossover)Single-dose per qualifying migraine attack (crossover)

Outcomes

OutcomeTypeControlInterventionHR / OR / RRP-value
Pain relief at 2 hours post-vaporization, defined as reduction of headache pain from moderate or severe to mild or none (per IHS guidelines); attacks without 2-hour data counted as failures in ITTPrimaryPlacebo: 46.6% (mITT)THC+CBD: 67.2%; THC-dominant: 68.9%; CBD-dominant: 52.6% (all mITT)2.85THC+CBD: p=0.016; THC-dominant: p=0.008; CBD-dominant: p>0.05
SecondaryPlacebo: 15.5%THC+CBD: 34.5% (OR 3.30 [1.24–8.80], p=0.017); THC-dominant and CBD-dominant not superior to placebo
SecondaryPlacebo: 34.5%THC+CBD: 60.3% (OR 3.32 [1.45–7.64], p=0.005); THC-dominant and CBD-dominant not superior to placebo
SecondaryPlacebo: 10.7%THC+CBD: 28.0% (OR 3.45 [1.14–10.50], p=0.029); THC-dominant and CBD-dominant not different from placebo
SecondaryPlacebo: 25.0%THC+CBD: 46.0% (OR 2.83 [1.10–7.26], p=0.031); THC-dominant and CBD-dominant not different from placebo
SecondaryPlacebo: 18.4%THC+CBD: 39.6% (OR 3.39 [1.24–9.32], p=0.018); THC-dominant and CBD-dominant not different from placebo
SecondaryPlacebo: 10.2%THC+CBD: 22.9% (OR 2.77 [0.84–9.12], p=0.094, non-significant); THC-dominant and CBD-dominant not different from placebo
SecondaryPlacebo: 36.7%THC+CBD: 53.6% (OR 2.56 [1.05–6.25], p=0.039); THC-dominant: 65.5% (OR 4.72 [1.89–11.81], p<0.001); CBD-dominant: 58.9% (OR 3.20 [1.31–7.82], p=0.011); all three active arms superior
SecondaryPlacebo: 5.0%THC-dominant: 17.2% (OR 4.90 [1.12–21.34], p=0.034); THC+CBD and CBD-dominant not superior to placebo
SecondaryPlacebo: 21.7%THC-dominant: 37.9% (OR 2.68 [1.06–6.79], p=0.038); CBD-dominant: 41.1% (OR 3.10 [1.21–7.91], p=0.018); THC+CBD: 33.9% (OR 2.19 [0.85–5.64], p=0.103, NS)
SecondaryTHC+CBD superior to placebo; THC-dominant and CBD-dominant not superior
SecondaryTHC+CBD superior to placebo; THC-dominant and CBD-dominant not superior
SecondaryNo treatment arm superior to placebo for nausea or vomiting
Safety
Safety
Safety
Safety
NoneAdverse
Subjective Highness at 1 Hour (mean out of 10)Adverse
Full AE data in Table 2; THC-dominant had greatest psychoactive burden; full AE table not reproduced in available source textAdverse

Subgroup Analysis

Results consistent across ITT, mITT, and sensitivity analyses for primary and secondary endpoints. Adjusting for treatment session number did not alter results. Study included both episodic (72.5%) and chronic (27.5%) migraine patients, improving generalizability over prior acute migraine RCTs that excluded chronic migraine.


Criticisms

  • Single-center study (UCSD) limits generalizability
  • Only one potency of THC (6%) and CBD (11%) and one THC:CBD ratio studied; no dose-response data available
  • NIDA-supplied cannabis lacked terpenes and minor cannabinoids; findings may not generalize to commercially available products
  • Crossover design: not all 92 enrolled participants completed all 4 treatment arms (73 contributed to ITT)
  • No assessment of long-term use, repeated dosing, medication overuse headache risk, or cannabis use disorder risk
  • Preprint — not peer-reviewed at time of medRxiv posting
  • Participants required to withhold other acute migraine treatments for 2 hours post-dose, which may not reflect real-world practice
  • Blinding partially challenged by psychoactive effects of THC, though formal blinding assessment showed near-chance treatment identification rates

Funding

Migraine Research Foundation (stated in partial acknowledgements; full funding statement was truncated in available source text)

Based on: CANNABIS MIGRAINE (medRxiv (preprint), 2024)

Authors: Nathaniel M. Schuster, Mark S. Wallace, Thomas D. Marcotte, ..., Michelle Sexton

Citation: Schuster NM, Wallace MS, Marcotte TD, Buse DC, Lee E, Liu L, Sexton M. Vaporized Cannabis versus Placebo for Acute Migraine: A Randomized Controlled Trial. medRxiv. 2024. doi:10.1101/2024.02.16.24302843

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